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RT @FrontNeurosci: New Research: White Matter Pathology as a Barrier to Gangliosidosis Gene Therapy: The gangliosidoses are a family of neu…
RT @FrontNeurosci: New Research: White Matter Pathology as a Barrier to Gangliosidosis Gene Therapy: The gangliosidoses are a family of neu…
New Research: White Matter Pathology as a Barrier to Gangliosidosis Gene Therapy: The gangliosidoses are a family of neurodegenerative lysosomal storage diseases that have recently seen promising advances in gene therapy. White matter… https://t.co/qhg4pnH