Analysis of effect of enzyme replacement therapy in 18 patients of Pompe disease
Article in Chinese Journal of Neurology (May 2024)
The most recent citing publications are shown below. View all 6 publications that cite this research output on Dimensions.
Efficacy and safety of enzyme replacement therapy with alglucosidase alfa for the treatment of patients with infantile-onset Pompe disease: a systematic review and metanalysis
Article in Frontiers in Pediatrics (February 2024)
Higher dose alglucosidase alfa is associated with improved overall survival in infantile-onset Pompe disease (IOPD): data from the Pompe Registry
Article in Orphanet Journal of Rare Diseases (December 2023)