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RT @FrontCVMedicine: New Research: Pompe disease in China: clinical and molecular characteristics: Background Pompe disease (PD) is a rare…
RT @FrontCVMedicine: New Research: Pompe disease in China: clinical and molecular characteristics: Background Pompe disease (PD) is a rare…
New Research: Pompe disease in China: clinical and molecular characteristics: Background Pompe disease (PD) is a rare, progressive, and autosomal recessive lysosomal storage disorder caused by mutations in the acid α-glucosidase gene.… https://t.co/Rqf9Hx