Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
Article in Gene Therapy (March 2024)
The most recent citing publications are shown below. View all 4 publications that cite this research output on Dimensions.
Adoptive cell therapy for treatment of rare diseases and orphan designation.
Preprint in Research Square (December 2023)
Licensing of Orphan Medicinal Products—Use of Real-World Data and Other External Data on Efficacy Aspects in Marketing Authorization Applications Concluded at the European Medicines Agency Between 2019 and 2021
Article in Frontiers in Pharmacology (August 2022)